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Cell penetrating peptide Myotonic dystrophy Muscle RNA splicing ACETYLCHOLINESTERASE Cytoskeleton Glutamate RNA interference Neuron Knockout Myotonic dystrophy type 1 MBNL Trinucleotide repeat expansion Genotype phenotype correlation Thérapie génique CTG repeat contractions Aging Dilated cardiomyopathy Gene therapy Oligodendrocyte Heart Transgenic mouse Astrocytes Mice Dystrophin CMS CTG repeats PCR GABA Dystrophie myotonique Diaphragm Therapy GSK3␤ Antisense oligonucleotide Skeletal muscle Dystrophie Myotonique Myotonic Dystrophy type 1 Male Dynamin 2 RNA biology Brain dysfunction Myostatin Cardiac muscle Acetylcholinesterase knockout mouse Cell culture model Transcriptomics Centronuclear myopathy Antisense oligonucleotides Humans CONGENITAL MYATHENIC SYNDROME Brain DMPK Trinucleotide Repeat Expansion Motoneuron DM1 ARN Myotonic Dystrophy Mouse model Maximal force Alternative splicing Myotonic dystrophy mouse models Cell model Exercise PacBio Exercice Intermediate filament Autophagy Fibrosis Glial cells In vivo CRISPR/Cas9 KNOCKOUT MICE CRISPRi Acetylcholinesterase deficiency Expression Glucocorticoid-receptor Duchenne muscular dystrophy Endurance training Animals CTG repeat instability Acute coronary syndrome Long read sequencing Glucocorticoids Quantitative microdialysis Muscular dystrophy Heart failure Mouse models Hypoxia Myotonic Dystrophy Type 1 Myelin Oligodendrocytes Transgenic mouse model Astrocyte Desmin DMSXL mice BIOLOGIE MOLECULAIRE Central nervous system Gene Therapy Gene editing AAV